2Decisions
2Patient groups
Added benefit by patient group
Decisions, newest first
Each decision lists only the patient groups coded with this disease.
Non-quantifiable
Patienten aller Altersklassen mit nicht-neurologischer Krankheitsanzeichen der Mukopolysaccharidose VII (MPS VII; Sly-Syndrom)
Active substance
Vestronidase alfa
Appropriate comparator therapy
N/A
ICD codes
Diagnoses
- Mukopolysaccharidose Typ VII
Minor
Patienten aller Altersklassen mit Mucopolysaccharidose vom Typ IVA (Morquio A Syndrom, MPS IVA)
Active substance
Elosulfase alfa
Appropriate comparator therapy
N/A
ICD codes
Diagnoses
- Mukopolysaccharidose Typ IVa
Data status: 2026-10-29